"The new approved treatments available to Duchenne muscular dystrophy patients have the potential to slow the progression of this devastating disorder," said
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1. Treat-NMD. http://www.treat-nmd.eu/downloads/file/ meetings/2013/workshop/Session1/McDonald_NH.pdf. [Accessed
2. Ryder et al. Orphanet J Rare Dis. 2017; 12(1):79.
3. Wei Y et al. J of Neuromuscul Dis. 2015;2(3):313-324.
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